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LEADER: 09291cam 2201273Ia 4500
001 ocn711000622
003 OCoLC
005 20200506234253.0
008 110404s2010 dcua ob 001 0 eng d
006 m o d
007 cr cnu---unuuu
010 $a 2010052788
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020 $a9780309158077$q(electronic bk.)
020 $a0309158079$q(electronic bk.)
020 $a1283044560
020 $a9781283044561
020 $z9780309158060
020 $z0309158060
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050 4 $aRS420$b.R357 2010eb
060 00 $aQV 736$bR221 2010
072 7 $aMED$x023000$2bisacsh
072 7 $aMED$x071000$2bisacsh
072 7 $aMED$x072000$2bisacsh
072 7 $aMED$x058170$2bisacsh
082 04 $a615/.19$222
245 00 $aRare diseases and orphan products :$baccelerating research and development /$cCommittee on Accelerating Rare Diseases Research and Orphan Product Development, Board on Health Sciences Policy ; Marilyn J. Field and Thomas F. Boat, editors ; Institute of Medicine of the National Academies.
260 $aWashington, D.C. :$bNational Academies Press,$c℗♭2010.
300 $a1 online resource (xxi, 420 pages) :$billustrations
336 $atext$btxt$2rdacontent
337 $acomputer$bc$2rdamedia
338 $aonline resource$bcr$2rdacarrier
504 $aIncludes bibliographical references (pages 249-282) and index.
505 0 $aProfile of rare diseases -- Regulatory framework for drugs for rare diseases -- Discovery research for rare diseases and orphan product development -- Development of new therapeutic drugs and biologics for rare diseases -- Coverage and reimbursement : incentives and disincentives for product development -- Medical devices : research and development for rare diseases -- Toward an integrated approach to accelerating research and product development for rare diseases.
588 0 $aPrint version record.
520 $a"Rare diseases collectively affect millions of Americans of all ages, but developing drugs and medical devices to prevent, diagnose, and treat these conditions is challenging. The IOM recommends implementing an integrated national strategy to promote rare diseases research and product development."--Publisher's description.
650 0 $aOrphan drugs.
650 0 $aDrugs$xDesign.
650 0 $aRare diseases$xTreatment.
650 12 $aOrphan Drug Production$vEvaluation Studies.
650 12 $aRare Diseases$xdrug therapy$vEvaluation Studies.
650 22 $aDrug Discovery$vEvaluation Studies.
650 22 $aDrug Evaluation$vEvaluation Studies.
650 22 $aHealth Policy$vEvaluation Studies.
650 22 $aPolicy Making$vEvaluation Studies.
650 7 $aMEDICAL$xDrug Guides.$2bisacsh
650 7 $aMEDICAL$xPharmacology.$2bisacsh
650 7 $aMEDICAL$xPharmacy.$2bisacsh
650 7 $aMEDICAL$xNursing$xPharmacology.$2bisacsh
650 7 $aDrugs$xDesign.$2fast$0(OCoLC)fst00898790
650 7 $aOrphan drugs.$2fast$0(OCoLC)fst01048416
655 0 $aElectronic books.
655 4 $aElectronic books.
700 1 $aField, Marilyn J.$q(Marilyn Jane)
700 1 $aBoat, Thomas F.
710 2 $aInstitute of Medicine (U.S.).$bCommittee on Accelerating Rare Diseases Research and Orphan Product Development.
776 08 $iPrint version:$tRare diseases and orphan products.$dWashington, D.C. : National Academies Press, ℗♭2010$z9780309158060$w(DLC) 2010052788$w(OCoLC)681488330
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856 40 $3National Academies Press$uhttp://www.nap.edu/catalog.php?record_id=12953
856 40 $3National Academies Press$uhttp://books.nap.edu/openbook.php?record_id=12953
856 40 $3National Academies Press$uhttp://www.nap.edu/catalog.php?record_id=12953#toc
856 40 $3National Academies Press$uhttp://www.nap.edu/openbook.php?record_id=12953
856 40 $3ProQuest Ebook Central$uhttp://public.ebookcentral.proquest.com/choice/publicfullrecord.aspx?p=3378753
856 40 $uhttps://www.ncbi.nlm.nih.gov/books/NBK56189
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856 40 $3Red Deer College Access$uhttp://ebookcentral.proquest.com/lib/rdc/detail.action?docID=3378753$z(Unlimited Concurrent Users)$zfrom Ebook Central Academic Complete
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856 40 $uhttps://ebookcentral.proquest.com/lib/ben/detail.action?docID=3378753$yLink to Rare diseases and orphan products$z(access limited to Benedictine University patrons)
856 40 $uhttps://ebookcentral.proquest.com/lib/uvic/detail.action?docID=3378753
856 40 $zVIEW FULL TEXT$uhttp://VH7QX3XE2P.search.serialssolutions.com/?V=1.0&L=VH7QX3XE2P&S=JCs&C=TC0000472566&T=marc&tab=BOOKS
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